The next generation of gene therapy is here. Let's end genetic disease. Make a tax-deductible donation today.
We've launched our end of year #Match4Riaan Campaign! Donate by December to double your impact. All gifts up to $100,000 will be matched - dollar for dollar.
We have ambitious, time-sensitive goals, and appreciate your generous donations to move with the urgency we need to support translational scientific research that can save the lives of Riaan and many other children. Help us raise four million dollars to accelerate and fund CSA gene replacement therapy, and other treatments for Cockayne Syndrome. Children diagnosed with Cockayne Syndrome often have very short life spans so we are racing against the clock.